Resources & References

1️⃣ References

1. National Organization for Rare Disorders (NORD)

2. Orphanet – The Rare Disease Database

3. PubMed – Rare Disease Research

4. rarediseases.org/news 

5. My Cleveland Clinic 

6. Medical News Today 

7. Labiotech 

2️⃣ Government & Regulatory Bodies

1. U.S. Food & Drug Administration (FDA) – Orphan Drugs

2. European Medicines Agency (EMA) – Rare Diseases

3. World Health Organization (WHO) – Rare Diseases

3️⃣ Patient Support & Advocacy Groups

1. Global Genes – Rare Disease Support

2. Rare Disease UK

3. EveryLife Foundation for Rare Diseases

4. Pace Hospital